Sarepta Therapeutics(美國)

Sarepta Therapeutics

美國SareptaTherapeutics www.sareptatherapeutics.com公司是一家生物制藥公司，研究和開發(fā)以抗轉(zhuǎn)錄療法和癌癥免疫療法技術(shù)為基礎(chǔ)的治療性產(chǎn)品.該公司成立于1980年，總部在美國華盛頓， isfocusedondevelopingfirst-in-classRNA-basedtherapeuticstoimproveandsavethelivesofpeop leaffectedbyseriousandlife-threateningrareandinfectiousdiseases.TheCompany'sdiversepipelineincludesitsleadprogrameteplirsen,forDuchennemusculardystrophy,aswellaspotentialtreatmentsforsomeoftheworld'smostlethalinfectiousdiseases.Sareptaaimstobuildaleading,independentbiotechcompanydedicatedtotranslatingitsRNA-basedscienceintotransformationaltherapeuticsforpatientswhofacesignificantunmetmedicalneeds.